Castuner

RARECast

RARECast

RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.

Podcast website

Listen in your app

Episodes

620 episodes

  1. The Invisible Burden of a Rare Liver Disease 32:26
  2. Yearning for Normal 40:28
  3. Building Better Rare Disease Data 33:37
  4. Using AI to Help Patients Get the Care They Need 33:50
  5. Targeting Immune Dysfunction in ALS 39:47
  6. When the Patient Is Left to Connect the Dots 52:21
  7. Enabling Patient Foundations to Build the Next Generation of Genetic Therapies 38:39
  8. Using Exosomes to Tackle the Delivery Challenge of Genetic Medicines for the Brain 27:08
  9. Building a Roadmap to Treat a Rare Neurodevelopmental Condition 33:55
  10. The Long Road from the NICU to New Therapies 52:42
  11. Stopping Guillain-Barré Syndrome at Its Source 39:13
  12. From Repeated Surgery to a Precision Patch 34:56
  13. Curing Sickle Cell Before Life Begins 30:56
  14. Spotting Neuromuscular Red Flags 37:08
  15. Expanding into a Global Rare Disease Player through Deal-Driven Innovation 51:57
  16. When Geography, Cost, and Policy Become as Life-Limiting as a Disease 36:20
  17. A One-Time Cell Therapy to Reset the Immune System in Autoimmune Diseases 36:49
  18. Building the Infrastructure for Made‑to‑Order Gene Therapies 35:49
  19. Rewiring the Rare Disease Diagnostic Odyssey 38:11
  20. Emerging from a Life in the Shadows 36:36
  21. Fitting Big Genes into Small Vectors 33:24
  22. Targeting Iron Dysregulation in the Neurodegenerative Condition MSA 33:09
  23. Long Reads, Shorter Journeys 35:23
  24. The Critical Role of Patient Community-Industry Partnership in Advancing a Gene Therapy 46:20
  25. Capturing the Lived Experience of Rare Disease 39:57
  26. Raising Awareness of Clinical Trials 36:30
  27. Using AI and Longitudinal Data to Transform Rare Disease Care 19:21
  28. Cutting through the Diagnostic Maze for Rare Diseases 38:56
  29. How Parents Took Development of a Gene Therapy into Their Own Hands 45:41
  30. Matching the Right Therapy to the Right Child with a Rare Cancer 45:47
  31. From Treating Symptoms to Addressing Causes in Rare Autoimmune Diseases 23:40
  32. A Mother’s Journey to Rewrite a Neurodevelopmental Disorder 57:13
  33. How a Foundation Built Its Own Drug Program for an Ultra-Rare Disease 35:50
  34. From Bloodletting to Breakthroughs in PV 36:30
  35. When Endpoints Miss the Point 36:47
  36. Reopening the Developmental Window in Rett Syndrome with a Gene Therapy 40:52
  37. A Data Strategy to Capitalize on a Multi Trillion Dollar Opportunity 26:16
  38. When a Gene Echoes Through a Family 31:15
  39. Changing the Autoimmune Disease Playbook with RNA-Engineered CAR T Cells 22:11
  40. Rewriting Rare Disease R&D with Foundation Models 26:30
  41. Resetting Aberrant Tregs Epigenetically to Treat Autoimmune Diseases 30:19
  42. Finding a Ready Treatment for a Newly Discovered, Ultra-Rare Disease 32:40
  43. One Rare Mother’s Quest to Rewrite Her Son’s Future with a Gene Therapy 35:46
  44. Transforming TSC Epilepsy with a Precision Therapy 25:06
  45. Bridging the Valley for Rare Disease Drug Development 41:36
  46. Turning a Rare Cancer into a Call to Action 42:53
  47. Developing a New Approach to Cystic Fibrosis to Improve Outcomes 29:31
  48. Finding Strength in Weakness 25:50
  49. Developing Targeted Therapies for a Rare Autoimmune Disease 37:41
  50. A Venture Fund that Leverages Patient Experts to Target Autoimmune Diseases 31:01